A New Zealand chemist is on the brink of history, with her breakthrough treatment for Rett Syndrome.
Distinguished Professor Dame Margaret Brimble and her team has been working on the drug for 20 years.
They expect to hear within days whether their treatment Trofinetide has been granted final approval by the US Food and Drug Administration.
Brimble told Mike Hosking it'll be a life changer for babies born with the syndrome.
The disorder impacts almost exclusively females, and stalls motor control and communications in infants.
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